EFTA01110707Set 9
22p7,189w
Behavioral Neurobiology,
CONCORDIA UNIVERSITY, Montreal, Canada
1993-1995 Postdoctoral Research Fellow
Section of Neurosurgery,
Gene Therapy and Neurogenetics Laboratories
YALE UNIVERSITY, New Haven, USA
1995-1998 Research Scientist
Department ... Neurosurgery,
Gene Therapy and Neurogenetics Laboratories
YALE UNIVERSITY, New Haven, USA
1997-1998 Visiting Scientist
Gene Therapy Center
Department of Molecular Medicine
UNIVERSITY OF AUCKLAND, Auckland, New Zealand ... JEFFERSON MEDICAL COLLEGE, Philadelphia, PA, USA
EFTA01110707
LEONE, Paola
1998-2001 Associate Director
CNS Gene Therapy Center
JEFFERSON MEDICAL COLLEGE, Philadelphia, PA, USA
2002-2007 Associate Professor
Department of Surgery
https://www.justice.gov/epstein/files/DataSet%209/EFTA01110707.pdf
EFTA01100261Set 9
2016-02-2939p20,086w
genetic diseases. This approach differs Prior ModelWare EPS
(1)
from the more commonly known gene therapy in that it can accurately remove P/E NM NM NM NM
and replace genes ... gene sequence without specificity Consensus EPS ($)1
Div yld (%)
as happens in gene therapy. Thus, the potential of CRISPR is broad with Unkst oihemiie noted, all metrics am based ... CRISPR has the best chance to
create durable, functional cures of many genetic diseases.
Gene therapy vs Gene editing?
Gene therapy differs from gene editing in both the approach
https://www.justice.gov/epstein/files/DataSet%209/EFTA01100261.pdf
EFTA00689626Set 9
2015-06-163p994w
Ariane Dwyer , Paul
Morris Stewart Oldfield , Richard Kahn
Subject: AAVL: (BN) Avalanche Drops as Gene Therapy Trial Miss High Expectation [C]
Date ... mailto:stepvah@bloomberg.net]
Sent: Tuesday, June 16, 2015 9:41AM
Subject: (BN) Avalanche Drops as Gene Therapy Trial Miss High Expectation
(BN) Avalanche Drops as Gene Therapy Trial Miss High Expectation ... subject to change without notice. Additional information is available upon
request.
Avalanche Drops as Gene Therapy Trial Miss High Expectations (1)
2015-06-15 21:36:53.569 GMT
(Updates with
https://www.justice.gov/epstein/files/DataSet%209/EFTA00689626.pdf
EFTA00603134Set 9
2p1,966w
JohnP.A.loannklis.
MD.D5c of search terms that include gene, genome, stem cells, Continued enthusiasm for gene therapy ignores
StanfordPrevention or regenerative medicine.' These topics have also in- what is known from ... genetic defect, no targeted therapy has
1196 110), but articles identified with gene therapy or stem emerged for sickle cell anemia.
cell increased by 874% (2635 to 25 662)and752
https://www.justice.gov/epstein/files/DataSet%209/EFTA00603134.pdf
Barre-Sinoussl, • Alzheimer's Disease:
Nobel Prize in Medicine in 2008 the hope for gene therapy
At the Atomic Energy Commission, INSERM Director
Jean Weissenbach, of Research Nathalie Cartier ... progres-
CNRS Gold Medal in 2008 and sion of Alzheimer's Disease through gene therapy (a
Foundation for Medical Research method using genes and the information carried wit-
Grand Prize
https://www.justice.gov/epstein/files/DataSet%209/EFTA00592853.pdf
EFTA02705187Set 11
2014-12-316p1,300w
that may include analysis of personalized genomics, microbiomics, metabolomics, and other
omics; development of gene therapies; engineering cells resistant to viruses; aging reversal;
humanized animals for research and organ transplants ... possible could include analysis of
personalized genomics, microbiomics, metabolomics, and other omics; development of
gene therapies; engineering cells resistant to all viruses; aging reversal; humanized animals
for research and organ
https://www.justice.gov/epstein/files/DataSet%2011/EFTA02705187.pdf